Vamorolone (AGAMREE®) Information Sheet for Families
Vamorolone (AGAMREE®), is a new steroid used to treat Duchenne muscular dystrophy (DMD). It is designed to offer the same muscle-strengthening benefits as classic steroids—such as prednisone, prednisolone, and deflazacort—while potentially reducing some of the common side effects associated with these medications.
This information sheet has been prepared by OPTIMIZE DMD to help individuals living with DMD and their families better understand the role of Vamorolone in DMD treatment.
For more information, please consult your healthcare provider.
Delayed Puberty & DMD
Dr. Claire Wood — co-chair of the OPTIMIZE DMD Growth & Puberty Working Group — in this short video, discusses delayed puberty in individuals with Duchenne Muscular Dystrophy (DMD).
Funded by Duchenne UK, this educational video highlights how long-term steroid use, a common treatment in DMD, can interfere with the body’s natural ability to begin puberty. In fact, most boys with DMD on daily steroids will not enter puberty without medical support.
📌 What you’ll learn:
- Why delayed puberty happens in DMD
- How it is diagnosed
- Management strategies and treatment options
Watch now to understand this important aspect of DMD care and learn how to better support boys navigating this stage of development.